Holiday Inn Kensington Forum, London, UK
http://www.orphandrugs.co.uk/PMMed
- Olivier Morand, Clinical Science Program Head, Actelion Pharmaceuticals
- Larissa Kerecuk, Rare Disease Lead, Consultant Paediatric Nephrologist, Birmingham Children’s Hospital
- Oliver Timmis, CEO, AKU Society
- Stuart Hughes, Director, Head of Pharmacology, Vertex
- Nadia Assenova, Senior Director Regulatory Affairs, EMEA, Alexion Pharma GmbH
- Christine Lavery, Group Chief Executive, MPS Society
- Hsin Loke, Director, Strategy, Operations and Finance, Rare Diseases Unit, GlaxoSmithKline
- Olaf Ritzeler, External Innovation Lead, Sanofi
- Stephen Marcus, CEO, Cantex Pharmaceuticals
- Kei Kishimoto, Chief Scientific Officer, Selecta Biosciences
- Learn about new therapies for different rare diseases, and how these can successfully be applied to other diseases with similar attributes
- Hear what opportunities and challenges come with working on rare diseases, as well as the development of the world’s first rare disease centre for children
- Expand your knowledge on patient collaboration and patient centric models with the stream on patient engagement, covering improvement strategies, patient-led trials, and much more
- Gather further insight on drug approval and reimbursement with MAA, and how techniques for drug repurposing in the rare disease area can help treatment
